RESTORING
MISSING
PROTEINS
RESTORING
THE
FUTURE
GenomeGo is pioneering a new way to treat the underlying causes of severe genetic diseases by precisely upregulating protein expression
RESTORING
MISSING
PROTEINS
RESTORING
THE
FUTURE
GenomeGo is pioneering a new way to treat the underlying causes
of severe genetic diseases by precisely upregulating protein expression
PROGRAMS
Hemoglobinopathies
Aiming to treat β-thalassemia and sickle cell disease with gene-edited hematopoietic stem cells
In vivo
Editing cells inside the body to treat genetically-defined diseases
Immuno-Oncology
Creating the next generation of cell therapies for cancer enabled by gene editing
Regenerative treatment
Broadening the applications of stem cells through gene editing
The Power of GenomeGO
Treating severe or life threatening genetic based diseases requires safe, durable, and effective therapies. GenomeGO harnesses key features of gene editing and gene therapy to develop powerful, tailored therapies for individual genetic diseases.
