RESTORING
MISSING
PROTEINS

RESTORING
THE
FUTURE

GenomeGo is pioneering a new way to treat the underlying causes of severe genetic diseases by precisely upregulating protein expression

RESTORING
MISSING
PROTEINS

RESTORING
THE
FUTURE

GenomeGo is pioneering a new way to treat the underlying causes
of severe genetic diseases by precisely upregulating protein expression

PROGRAMS

Hemoglobinopathies

Aiming to treat β-thalassemia and sickle cell disease with gene-edited hematopoietic stem cells

In vivo

Editing cells inside the body to treat genetically-defined diseases

Immuno-Oncology

Creating the next generation of cell therapies for cancer enabled by gene editing

Regenerative treatment

Broadening the applications of stem cells through gene editing

The Power of GenomeGO

Treating severe or life threatening genetic based diseases requires safe, durable, and effective therapies. GenomeGO harnesses key features of gene editing and gene therapy to develop powerful, tailored therapies for individual genetic diseases.

  • Designed with reverse complement coding sequences

  • Potential to significantly improve integration, leading to increased efficacy

  • Broad patent filings covering GenomeGO templates

  • Designed to maximize efficiency of DNA corrections

  • Provides ability to address larger patient populations